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ECHO

CompletedPhase 3Results posted

Energy Balance & Weight Loss in Craniopharyngioma-related or Other Hypothalamic Tumors in Hypothalamic Obesity

Glucagon-Like Peptide-1 Agonist Effects on Energy Balance in Hypothalamic Obesity

Assets

Exenatide / GLP-1 / incretin class catch-all

Listed sites

3

Recruiting sites

Enrollment

42

actual

Study population

Hypothalamic / syndromic obesity, Obesity / overweight

Key I/E criterion

BMI ≥95

Primary endpoint

BMI, change

Footprint

Where this trial recruits

Site locations as reported to ClinicalTrials.gov. Site count is not enrollment count; per-site enrollment is not available from source.

Identifiers

Registered as

NCT IDNCT02664441
Org study IDR01DK104936-01A1

Timeline

Milestones

Study first posted2016-01-27estimated
Primary completion2020-03-16actual
Study completion2020-07-31actual
Last update posted2022-05-05actual
Results first posted2022-05-05actual
Study start2016-03 (month precision)

Assets

Investigational agents

Study populations

Who this study enrolls

Hypothalamic / syndromic obesityObesity / overweight

Eligibility

Who can enroll

Minimum age10 Years
Maximum age25 Years
SexAll
Healthy volunteersNot accepted

Inclusion criteria

Age 10-25 years at time of enrollment
Diagnosis of hypothalamic obesity with age- and sex adjusted BMI ≥ 95% or BMI ≥30 kg/m² if over 18 y
History of craniopharyngioma or another tumor located in the hypothalamic area
Hypothalamic lesion documented by neuroradiology
≥ 6 months post-surgical or radiation treatment
Weight stable or increasing over 3 months prior to screening visit
Stable hormone replacement for at least 3 months prior to screening visit

Exclusion criteria

Renal impairment (GFR<60 ml/min/1.73m² using the Schwarz formula)
History of gastroparesis; pancreatitis or gallstones (unless status post cholecystectomy)
Family history of multiple endocrine neoplasia type 2 or familial medullary thyroid carcinoma metabolic disorders
Any insulin-treated diabetes mellitus, poorly controlled type 2 diabetes (HbA1c ≥ 10%), or any other chronic serious medical conditions such as cardiovascular disease, malignancy or hematologic disorder, complicated syndromic disorder, or psychiatric disorders (schizophrenia, major depression, history of suicide attempts)
Calcitonin >50 mg/L at screening
Initiation of weight loss medications within 3 months of screening visit
Previous donation of blood >10% of estimated blood volume within 3 months prior study
Current warfarin use
Current use of any other GLP1 receptor agonist
Untreated thyroid disorder or adrenal insufficiency
History of bariatric surgery or planned bariatric surgery until end of study
Pregnancy, lactation or expectation to conceive during study period
Subject unlikely to adhere to study procedures in opinion of investigator
Subject with contraindication to neuroimaging by MRI

Endpoints (11)

What's being measured

Protocol endpoints and posted registry outcome measures, grouped into outcome categories. Composite endpoints show their component event types. Standard codes (LOINC, SNOMED CT) are shown where available.

Coverage by outcome category

Weight & body composition
3
Glycemic / diabetes
3
Cardiometabolic biomarkers
3
Other clinical outcomes
2

Weight & body composition

3 endpoints
Primary/protocol endpoint

Percent Change of Body Mass Index (BMI) as Calculated by the Formula: Body Weight in kg Divided by Height in Meters².

Time frame:From baseline to 36 weeks

BMI, change

percent change from baseline, improvement

Posted result

GroupValue (mean), percent change from baseline95% CI
Exenatide Once Weekly Extended-release1.7
Matching Placebo3.5
Mean Difference (Net)-1.795% CI-4.10.6p0.40Mixed Models Analysis
Secondary/protocol endpoint

Changes in Body Composition as Assessed by Body Fat Mass Using Dual Energy X-ray Absorptiometry (DEXA)

Time frame:At baseline and 36 weeks

Total fat mass

change from baseline, improvement

Posted result

GroupValue (mean), kilograms95% CI
Exenatide Once Weekly Extended-release1.5
Matching Placebo4.6
Mean Difference (Net)-3.195% CI-5.7-0.4p0.02Mixed Models Analysis
Secondary/protocol endpoint

Changes of Energy Expenditure Assessed by Doubly Labeled Water Analysis

Time frame:Baseline and 36 weeks

total energy expenditure DLW

change from baseline, improvement

Posted result

GroupValue (mean), kcals/day95% CI
Exenatide Once Weekly Extended-release-17.8
Matching Placebo146.3
Mean Difference (Net)-166.495% CI-269.7-63.1p0.004Regression, Linear

Glycemic / diabetes

3 endpoints
Secondary/protocol endpoint

Changes in Fasting Glucose

Time frame:From baseline to 36 weeks

Fasting glucose, change

change from baseline, improvement

LOINC 1558-6

Posted result

GroupValue (mean), mg/dL95% CI
Exenatide Once Weekly Extended-release7.4
Matching Placebo3.7
Geometric Mean Ratio1.4295% CI0.972.08p0.19Mixed Models Analysis
Secondary/protocol endpoint

Changes of Insulin Resistance Assessed by Homeostasis Model Assessment of Insulin Resistance (HOMA-IR)

Time frame:From baseline to 36 weeks

HOMA-IR (insulin sensitivity)

change from baseline, improvement

Posted result

GroupValue (mean), HOMA-IR score95% CI
Exenatide Once Weekly Extended-release3.5
Matching Placebo2.2
Geometric Mean Ratio1.3995% CI0.902.14p0.32Mixed Models Analysis
Secondary/protocol endpoint

Changes in Glucose 120 Minutes Following an Oral Glucose Tolerance Test

Time frame:From baseline to 36 weeks

Postprandial glucose

change from baseline, improvement

Posted result

GroupValue (mean), mg/dL95% CI
Exenatide Once Weekly Extended-release-12.4
Matching Placebo-3.4
Mean Difference (Net)-8.595% CI-19.12.1p0.088Mixed Models Analysis

Cardiometabolic biomarkers

3 endpoints
Secondary/protocol endpoint

Changes in HDL Cholesterol and Triglycerides Assessed by Fasting Lipids

Time frame:From baseline to 36 weeks

change from baseline, improvement

componentsHDL-C, change, Triglycerides, change

Posted result

GroupValue (mean), mg/dL95% CI
Exenatide Once Weekly Extended-releaseHDL Cholesterol0.7
Triglycerides-0.6
Matching PlaceboHDL Cholesterol0.6
Triglycerides4.2
Geometric Mean Ratio1.0095% CI0.911.11p0.82Mixed Models Analysis

Analysis for HDL Cholesterol

Geometric Mean Ratio1.0095% CI0.831.19p0.92Mixed Models Analysis

Analysis for Triglycerides

Secondary/protocol endpoint

Changes in Inflammation Assessed by C-reactive Protein (CRP)

Time frame:From baseline to 36 weeks

hs-CRP, change

change from baseline, improvement

LOINC 30522-7

Posted result

GroupValue (mean), mg/dL95% CI
Exenatide Once Weekly Extended-release0.00
Matching Placebo0.18
Geometric Mean Ratio0.6295% CI0.410.92p0.03Mixed Models Analysis
Secondary/protocol endpoint

Changes of Circulating Leptin Levels

Time frame:From baseline to 36 weeks

Leptin, change

change from baseline, improvement

Posted result

GroupValue (mean), ng/mL95% CI
Exenatide Once Weekly Extended-release1.4
Matching Placebo11.8
Geometric Mean Ratio0.9595% CI0.811.10p0.69Mixed Models Analysis

Other clinical outcomes

2 endpoints
Secondary/protocol endpoint

Changes in Fat and Total Calorie Intake Assessed by Free Buffet Meal Analysis.

Time frame:From baseline to 36 weeks

change from baseline, improvement

componentsfat intake, total calorie intake

Posted result

GroupValue (mean), grams95% CI
Exenatide Once Weekly Extended-releaseFat Intake-9.5
Total Calorie Intake-287
Matching PlaceboFat Intake14.5
Total Calorie Intake224
Mean Difference (Final Values)-20.295% CI-37.8-2.7p.032Regression, Linear

Analysis for Fat Intake

Mean Difference (Net)-43095% CI-761-100p.02Regression, Linear

Analysis for Total Calorie Intake

Secondary/protocol endpoint

Changes of Energy Intake Assessed by Automated Self-Administered 24-Hour Dietary Recall (ASA24-Kids)

Time frame:Baseline and 36 weeks

change from baseline, descriptive

Posted result

GroupValue (mean), kcals95% CI
Exenatide Once Weekly Extended-release-62
Matching Placebo-210
Mean Difference (Net)-145.095% CI-653.5363.4p0.58Regression, Linear

Provenance

Sources

Trial identity, design, statusClinicalTrials.gov API v2
Snapshot dateJuly 1, 2026
Endpoint classificationDelfa endpoint taxonomy v2 (May 13, 2026)
Results tableClinicalTrials.gov results section

Trial facts come from public ClinicalTrials.gov records. Endpoint categories are Delfa's classification of those records, not a ClinicalTrials.gov field. All figures reflect the July 1, 2026 snapshot.